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Lysosomal Acid Lipase Deficiency - 25 Studies Found
Estado | Estudiar |
No longer available |
Nombre del estudio: An Expanded Access Protocol for Sebelipase Alfa for Patients With Lysosomal Acid Lipase Deficiency Condición: Lysosomal Acid Lipase Deficiency Fecha: 2015-02-25 Intervenciones: Drug: sebelipase alfa Other Name: SBC-102, recombinant human lysosomal acid lipase, rhLAL |
Active, not recruiting |
Nombre del estudio: Screening for Lysosomal Acid Lipase Deficiency Condición: Lysosomal Acid Lipase Deficiency Fecha: 2016-10-04 Intervenciones: Other: There is no intervention in the study |
Active, not recruiting |
Nombre del estudio: Safety and Efficacy Study of Sebelipase Alfa in Patients With Lysosomal Acid Lipase Deficiency Condición: Lysosomal Acid Lipase Deficiency Fecha: 2014-03-20 Intervenciones: Drug: sebelipase alfa Intravenous infusion of sebelipase alfa: 1mg/kg every other week |
Active, not recruiting |
Nombre del estudio: Clinical Trial in Infants With Rapidly Progressive Lysosomal Acid Lipase Deficiency Condición: Lysosomal Acid Lipase Deficiency Fecha: 2014-07-07 Intervenciones: Drug: sebelipase alfa Sebelipase alfa is a recombinant human lysosomal acid lipase (rhLAL). The investig |
Completed |
Nombre del estudio: A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype Condición:
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Terminated |
Nombre del estudio: Children With Lysosomal Acid Lipase Deficiency Who Previously Received Treatment With SBC-102 Condición:
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Active, not recruiting |
Nombre del estudio: SurVival of Lysosomal Acid Lipase Deficiency (LAL-D) Infants Treated With SebelipAse aLfa Condición:
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Active, not recruiting |
Nombre del estudio: Identification of Undiagnosed Lysosomal Acid Lipase Deficiency Condición:
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Active, not recruiting |
Nombre del estudio: A Multicenter Study of SBC-102 (Sebelipase Alfa) in Patients With Lysosomal Acid Lipase Deficiency/ ARISE (Acid Lipase Replacement Investigating Safety and Efficacy) Condición:
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Completed |
Nombre del estudio: Safety, Tolerability and Pharmacokinetics of SBC-102 (Sebelipase Alfa) in Adult Patients With Lysosomal Acid Lipase Deficiency Condición:
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